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About Us
Science
Base Editing
Base Editing Applications
Additional Technologies
Presentations and Publications
Pipeline
Patients
Commitment
Our Research
Expanded Access
Investors
Careers
Internships and Co-ops
Fellowships
Current Openings
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ESCAPE-2: Paired HSC CD117-epitope engineering and direct editing of sickle allele through base editing for antibody-mediated autologous HSC therapy conditioning for potential treatment of sickle cell anemia