About Us

Our vision is to provide life-long cures to patients suffering from serious diseases.

Our Values

To achieve our vision, we are continuing to build a strong, values-driven organization focused on our people, advancing cutting-edge science, and rigorously developing a new class of precision genetic medicines. Our values define how we work together:

A community of
fearless innovators
Rigorous and honest
in our research
Listening with
open minds
to each other

Executive and Scientific Leadership

Board of Directors

Founders and Inventors